Adeno-associated vectors . gene therapy products

Another interesting innovation is the registration of alipogene tiparvovec, it represents the first gene therapy treatment that has reached the market [15]. The medicinal product consists of the human lipoprotein lipase gene that is encapsulated in a vector derived from adeno-associated vims (AAV), serotype 1. The viral vector will deliver the gene into the cell, in this case a muscle cell, where the gene can be expressed after which the lipoprotein lipase is produced, fii... 

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